Oral Presentation ANZBMS-MEPSA-ANZORS 2022

Defining how vitamin D promotes tolerogenic dendritic cells to enable its use in combined therapy for multiple sclerosis and other autoimmune diseases. (#127)

Grant P Parnell 1 2 , Stephen D Schibeci 2 , Samantha Law 2 , David R Booth 2
  1. School of Medical Sciences, The University of Sydney, Sydney, NSW, Australia
  2. Centre for Immunology and Allergy Research, The Westmead Institute for Medical Research, Sydney, NSW, Australia

Background:

There is compelling genetic, laboratory and environmental evidence that vitamin D contributes to MS pathogenesis, but the inactive forms currently used in clinical trials have failed to provide benefit. This is because of genetic and epigenetic bottlenecks to vitamin D response.

Objective:

An improved approach is needed to obtain benefit from the vitamin D pathway. The objective of this study was to define how vitamin D promotes a tolerogenic phenotype in the immunological context most likely to underpin its benefit: control of dendritic cells. 

Methods:

We identified how the chromatin is remodelled using ATACseq (Assay for Transposase-Accessible Chromatin using sequencing) and global gene expression changes using RNAseq in response to treatment with calcipotriol (active vitamin D analogue) for monocyte-derived dendritic cells with a tolerogenic or inflammatory phenotype. We also characterised the effect of co-treatment with vitamin D and a novel bromodomain inhibitor, i-BRD9.

Results:

ATACseq revealed distinct chromatin accessibility changes in response to calcipotriol with over 4,000 genomic locations affected, accounting for approximately 8% of the variation in the ATACseq dataset. Transcriptomic analysis also showed a clear vitamin D response signature, with a far larger number of genes dysregulated in response to calcipotriol the inflammatory cells compared to the tolerogenic cells. Pathway analysis indicated a reduced inflammatory state in cells treated with calcipotriol.

Conclusions:

Calcipotriol treatment revealed a distinct a shift away from the inflammatory phenotype to a more immunosuppressive/tolerogenic phenotype. Work is ongoing to assess alternative strategies, including co-treatment with i-BRD9, to upregulate the vitamin D response and bypass the body’s homeostatic setpoint.